Clinical trial expertise
Indications we run clinical trials in
Evidence briefs for every indication — the approved therapies and their pivotal-trial endpoints, the magnitude of benefit, and the drugs that failed and why. A physician-led view of where each field stands.
Oncology
Oncology indications
Colorectal Cancer
ICD-10 C18.9 · approved drugs, endpoints & failures.
View →Cervical Cancer
ICD-10 C53.9 · approved drugs, endpoints & failures.
View →Endometrial (Uterine) Cancer
ICD-10 C54.1 · approved drugs, endpoints & failures.
View →Head & Neck Cancer (SCCHN)
ICD-10 C76.0 · approved drugs, endpoints & failures.
View →Oesophageal Cancer
ICD-10 C15.9 · approved drugs, endpoints & failures.
View →Hepatocellular Carcinoma
ICD-10 C22.0 · approved drugs, endpoints & failures.
View →Renal Cell Carcinoma
ICD-10 C64.9 · approved drugs, endpoints & failures.
View →Testicular Cancer
ICD-10 C62.90 · approved drugs, endpoints & failures.
View →Small-Cell Lung Cancer
ICD-10 C34.90 · approved drugs, endpoints & failures.
View →Non-Small-Cell Lung Cancer
ICD-10 C34.90 · approved drugs, endpoints & failures.
View →Cholangiocarcinoma
ICD-10 C22.1 · approved drugs, endpoints & failures.
View →Anal Cancer
ICD-10 C21.0 · approved drugs, endpoints & failures.
View →Vulvar Cancer
ICD-10 C51.9 · approved drugs, endpoints & failures.
View →Mesothelioma
ICD-10 C45.9 · approved drugs, endpoints & failures.
View →Neuroendocrine Tumours
ICD-10 C7A.00 · approved drugs, endpoints & failures.
View →Gastrointestinal Stromal Tumour (GIST)
ICD-10 C49.A0 · approved drugs, endpoints & failures.
View →Soft-Tissue Sarcoma
ICD-10 C49.9 · approved drugs, endpoints & failures.
View →Osteosarcoma
ICD-10 C41.9 · approved drugs, endpoints & failures.
View →Ewing Sarcoma
ICD-10 C41.9 · approved drugs, endpoints & failures.
View →Basal Cell Carcinoma
ICD-10 C44.91 · approved drugs, endpoints & failures.
View →Cutaneous Squamous Cell Carcinoma
ICD-10 C44.92 · approved drugs, endpoints & failures.
View →Merkel Cell Carcinoma
ICD-10 C4A.9 · approved drugs, endpoints & failures.
View →Nasopharyngeal Carcinoma
ICD-10 C11.9 · approved drugs, endpoints & failures.
View →Neuroblastoma
ICD-10 C74.90 · approved drugs, endpoints & failures.
View →Medulloblastoma
ICD-10 C71.6 · approved drugs, endpoints & failures.
View →Haematology-Oncology
Haematology-Oncology indications
Multiple Myeloma
ICD-10 C90.00 · approved drugs, endpoints & failures.
View →Chronic Lymphocytic Leukaemia (CLL)
ICD-10 C91.10 · approved drugs, endpoints & failures.
View →Acute Lymphoblastic Leukaemia (ALL)
ICD-10 C91.00 · approved drugs, endpoints & failures.
View →Chronic Myeloid Leukaemia (CML)
ICD-10 C92.10 · approved drugs, endpoints & failures.
View →Hodgkin Lymphoma
ICD-10 C81.90 · approved drugs, endpoints & failures.
View →Diffuse Large B-Cell Lymphoma (DLBCL)
ICD-10 C83.30 · approved drugs, endpoints & failures.
View →Follicular Lymphoma
ICD-10 C82.90 · approved drugs, endpoints & failures.
View →Mantle Cell Lymphoma
ICD-10 C83.10 · approved drugs, endpoints & failures.
View →Myelodysplastic Syndromes (MDS)
ICD-10 D46.9 · approved drugs, endpoints & failures.
View →Myelofibrosis
ICD-10 D47.4 · approved drugs, endpoints & failures.
View →Waldenström Macroglobulinaemia
ICD-10 C88.0 · approved drugs, endpoints & failures.
View →Hairy Cell Leukaemia
ICD-10 C91.40 · approved drugs, endpoints & failures.
View →Psychiatry
Psychiatry indications
Post-Traumatic Stress Disorder (PTSD)
ICD-10 F43.10 · approved drugs, endpoints & failures.
View →Obsessive-Compulsive Disorder (OCD)
ICD-10 F42.2 · approved drugs, endpoints & failures.
View →Social Anxiety Disorder
ICD-10 F40.10 · approved drugs, endpoints & failures.
View →Postpartum Depression
ICD-10 F53.0 · approved drugs, endpoints & failures.
View →Treatment-Resistant Depression
ICD-10 F33.2 · approved drugs, endpoints & failures.
View →Alcohol Use Disorder
ICD-10 F10.20 · approved drugs, endpoints & failures.
View →Opioid Use Disorder
ICD-10 F11.20 · approved drugs, endpoints & failures.
View →Anorexia Nervosa
ICD-10 F50.00 · approved drugs, endpoints & failures.
View →Autism Spectrum Disorder
ICD-10 F84.0 · approved drugs, endpoints & failures.
View →Insomnia Disorder
ICD-10 G47.00 · approved drugs, endpoints & failures.
View →Neurology
Neurology indications
Huntington's Disease
ICD-10 G10 · approved drugs, endpoints & failures.
View →Guillain-Barré Syndrome
ICD-10 G61.0 · approved drugs, endpoints & failures.
View →Chronic Inflammatory Demyelinating Polyneuropathy (CIDP)
ICD-10 G61.81 · approved drugs, endpoints & failures.
View →Neuromyelitis Optica Spectrum Disorder (NMOSD)
ICD-10 G36.0 · approved drugs, endpoints & failures.
View →Friedreich's Ataxia
ICD-10 G11.11 · approved drugs, endpoints & failures.
View →Essential Tremor
ICD-10 G25.0 · approved drugs, endpoints & failures.
View →Dystonia
ICD-10 G24.9 · approved drugs, endpoints & failures.
View →Restless Legs Syndrome
ICD-10 G25.81 · approved drugs, endpoints & failures.
View →Tourette Syndrome
ICD-10 F95.2 · approved drugs, endpoints & failures.
View →Neuromuscular
Neuromuscular indications
Spinal Muscular Atrophy (SMA)
ICD-10 G12.9 · approved drugs, endpoints & failures.
View →Duchenne Muscular Dystrophy
ICD-10 G71.01 · approved drugs, endpoints & failures.
View →Myotonic Dystrophy
ICD-10 G71.11 · approved drugs, endpoints & failures.
View →Myasthenia Gravis
ICD-10 G70.00 · approved drugs, endpoints & failures.
View →Cardiovascular
Cardiovascular indications
Hypertension
ICD-10 I10 · approved drugs, endpoints & failures.
View →Atrial Fibrillation
ICD-10 I48.91 · approved drugs, endpoints & failures.
View →Heart Failure with Preserved EF (HFpEF)
ICD-10 I50.30 · approved drugs, endpoints & failures.
View →Coronary Artery Disease
ICD-10 I25.10 · approved drugs, endpoints & failures.
View →Acute Coronary Syndrome
ICD-10 I24.9 · approved drugs, endpoints & failures.
View →Peripheral Artery Disease
ICD-10 I73.9 · approved drugs, endpoints & failures.
View →Pulmonary Embolism
ICD-10 I26.99 · approved drugs, endpoints & failures.
View →Hypertrophic Cardiomyopathy
ICD-10 I42.2 · approved drugs, endpoints & failures.
View →ATTR Cardiac Amyloidosis
ICD-10 E85.82 · approved drugs, endpoints & failures.
View →Aortic Stenosis
ICD-10 I35.0 · approved drugs, endpoints & failures.
View →Metabolic & Endocrine
Metabolic & Endocrine indications
Type 1 Diabetes
ICD-10 E10.9 · approved drugs, endpoints & failures.
View →Type 2 Diabetes
ICD-10 E11.9 · approved drugs, endpoints & failures.
View →MASH / NASH (Metabolic Steatohepatitis)
ICD-10 K75.81 · approved drugs, endpoints & failures.
View →Osteoporosis
ICD-10 M81.0 · approved drugs, endpoints & failures.
View →Gout
ICD-10 M10.9 · approved drugs, endpoints & failures.
View →Acromegaly
ICD-10 E22.0 · approved drugs, endpoints & failures.
View →Cushing's Disease
ICD-10 E24.0 · approved drugs, endpoints & failures.
View →Graves' Disease
ICD-10 E05.00 · approved drugs, endpoints & failures.
View →Polycystic Ovary Syndrome (PCOS)
ICD-10 E28.2 · approved drugs, endpoints & failures.
View →Respiratory
Respiratory indications
Severe Asthma
ICD-10 J45.50 · approved drugs, endpoints & failures.
View →Cystic Fibrosis
ICD-10 E84.9 · approved drugs, endpoints & failures.
View →Bronchiectasis
ICD-10 J47.9 · approved drugs, endpoints & failures.
View →Chronic Cough
ICD-10 R05.3 · approved drugs, endpoints & failures.
View →Chronic Rhinosinusitis with Nasal Polyps
ICD-10 J33.9 · approved drugs, endpoints & failures.
View →Obstructive Sleep Apnoea
ICD-10 G47.33 · approved drugs, endpoints & failures.
View →Sarcoidosis
ICD-10 D86.0 · approved drugs, endpoints & failures.
View →Alpha-1 Antitrypsin Deficiency
ICD-10 E88.01 · approved drugs, endpoints & failures.
View →Gastroenterology
Gastroenterology indications
Ulcerative Colitis
ICD-10 K51.90 · approved drugs, endpoints & failures.
View →Crohn's Disease
ICD-10 K50.90 · approved drugs, endpoints & failures.
View →Coeliac Disease
ICD-10 K90.0 · approved drugs, endpoints & failures.
View →Eosinophilic Oesophagitis
ICD-10 K20.0 · approved drugs, endpoints & failures.
View →Gastro-Oesophageal Reflux Disease (GERD)
ICD-10 K21.9 · approved drugs, endpoints & failures.
View →Gastroparesis
ICD-10 K31.84 · approved drugs, endpoints & failures.
View →Chronic Constipation
ICD-10 K59.09 · approved drugs, endpoints & failures.
View →Hepatitis C
ICD-10 B18.2 · approved drugs, endpoints & failures.
View →Primary Biliary Cholangitis
ICD-10 K74.3 · approved drugs, endpoints & failures.
View →Rheumatology
Rheumatology indications
Psoriatic Arthritis
ICD-10 L40.50 · approved drugs, endpoints & failures.
View →Axial Spondyloarthritis
ICD-10 M45.9 · approved drugs, endpoints & failures.
View →Systemic Lupus Erythematosus (SLE)
ICD-10 M32.9 · approved drugs, endpoints & failures.
View →Lupus Nephritis
ICD-10 M32.14 · approved drugs, endpoints & failures.
View →Sjögren's Syndrome
ICD-10 M35.00 · approved drugs, endpoints & failures.
View →Systemic Sclerosis (Scleroderma)
ICD-10 M34.9 · approved drugs, endpoints & failures.
View →ANCA-Associated Vasculitis
ICD-10 M31.31 · approved drugs, endpoints & failures.
View →Giant Cell Arteritis
ICD-10 M31.6 · approved drugs, endpoints & failures.
View →Dermatomyositis
ICD-10 M33.90 · approved drugs, endpoints & failures.
View →Hereditary Angioedema
ICD-10 D84.1 · approved drugs, endpoints & failures.
View →Dermatology
Dermatology indications
Hidradenitis Suppurativa
ICD-10 L73.2 · approved drugs, endpoints & failures.
View →Vitiligo
ICD-10 L80 · approved drugs, endpoints & failures.
View →Alopecia Areata
ICD-10 L63.9 · approved drugs, endpoints & failures.
View →Chronic Spontaneous Urticaria
ICD-10 L50.1 · approved drugs, endpoints & failures.
View →Rosacea
ICD-10 L71.9 · approved drugs, endpoints & failures.
View →Prurigo Nodularis
ICD-10 L28.1 · approved drugs, endpoints & failures.
View →Bullous Pemphigoid
ICD-10 L12.0 · approved drugs, endpoints & failures.
View →Ophthalmology
Ophthalmology indications
Diabetic Retinopathy
ICD-10 E11.319 · approved drugs, endpoints & failures.
View →Diabetic Macular Oedema
ICD-10 E11.311 · approved drugs, endpoints & failures.
View →Retinal Vein Occlusion
ICD-10 H34.8 · approved drugs, endpoints & failures.
View →Uveitis
ICD-10 H20.9 · approved drugs, endpoints & failures.
View →Dry Eye Disease
ICD-10 H04.129 · approved drugs, endpoints & failures.
View →Geographic Atrophy
ICD-10 H35.31 · approved drugs, endpoints & failures.
View →Retinitis Pigmentosa
ICD-10 H35.52 · approved drugs, endpoints & failures.
View →Infectious Disease
Infectious Disease indications
Influenza
ICD-10 J11.1 · approved drugs, endpoints & failures.
View →Respiratory Syncytial Virus (RSV)
ICD-10 J21.0 · approved drugs, endpoints & failures.
View →COVID-19
ICD-10 U07.1 · approved drugs, endpoints & failures.
View →Tuberculosis
ICD-10 A15.9 · approved drugs, endpoints & failures.
View →Malaria
ICD-10 B54 · approved drugs, endpoints & failures.
View →Clostridioides difficile Infection
ICD-10 A04.7 · approved drugs, endpoints & failures.
View →Sepsis
ICD-10 A41.9 · approved drugs, endpoints & failures.
View →Rare & Genetic
Rare & Genetic indications
Sickle Cell Disease
ICD-10 D57.1 · approved drugs, endpoints & failures.
View →Beta-Thalassaemia
ICD-10 D56.1 · approved drugs, endpoints & failures.
View →Haemophilia A
ICD-10 D66 · approved drugs, endpoints & failures.
View →Haemophilia B
ICD-10 D67 · approved drugs, endpoints & failures.
View →Gaucher Disease
ICD-10 E75.22 · approved drugs, endpoints & failures.
View →Fabry Disease
ICD-10 E75.21 · approved drugs, endpoints & failures.
View →Pompe Disease
ICD-10 E74.02 · approved drugs, endpoints & failures.
View →Wilson's Disease
ICD-10 E83.01 · approved drugs, endpoints & failures.
View →AL Amyloidosis
ICD-10 E85.81 · approved drugs, endpoints & failures.
View →Hereditary ATTR Amyloidosis
ICD-10 E85.1 · approved drugs, endpoints & failures.
View →Angelman Syndrome
ICD-10 Q93.51 · approved drugs, endpoints & failures.
View →Women’s Health
Women’s Health indications
Endometriosis
ICD-10 N80.9 · approved drugs, endpoints & failures.
View →Uterine Fibroids
ICD-10 D25.9 · approved drugs, endpoints & failures.
View →Menopausal Vasomotor Symptoms
ICD-10 N95.1 · approved drugs, endpoints & failures.
View →Heavy Menstrual Bleeding
ICD-10 N92.0 · approved drugs, endpoints & failures.
View →Pre-eclampsia
ICD-10 O14.90 · approved drugs, endpoints & failures.
View →Preterm Labour
ICD-10 O60.00 · approved drugs, endpoints & failures.
View →Urology
Urology indications
Overactive Bladder
ICD-10 N32.81 · approved drugs, endpoints & failures.
View →Benign Prostatic Hyperplasia
ICD-10 N40.0 · approved drugs, endpoints & failures.
View →Interstitial Cystitis
ICD-10 N30.10 · approved drugs, endpoints & failures.
View →Erectile Dysfunction
ICD-10 N52.9 · approved drugs, endpoints & failures.
View →Don't see your indication?
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